Intercept’s US president Vivek Devaraj said the pharma company still believes in the evidence supporting the liver disease ...

Karl Fitzpatrick has described his frightening ordeal after being diagnosed with potentially life-threatening Guillain–Barré ...

to use its artificial intelligence to identify novel rare disease indications for a discontinued drug asset. Under the terms of the agreement, Sanofi will provide data related to the unnamed drug ...

PTC Therapeutics (PTCT) stock on watch as company receives FDA approval for gene therapy Kebilidi for AADC deficiency. Read ...

but the scope of support has expanded as the "Rare Disease Control Act amendment" passed the National Assembly. Ji Young-mi, ...

On Wednesday, The Dallas Morning News reported that Dallas restauranteur Al Biernat died at 69 after a battle with ...

A Brisbane father has died a month after being diagnosed with an ultra-rare genetic condition that he dubbed the family “curse”. Lachlan Webb was diagnosed with the incurable genetic disease fatal ...

AstraZeneca’s growth was driven by its portfolio of products in the oncology, biopharmaceuticals and rare disease segments ...

Gurugram: Doctors at a private hospital in Haryana's Gurugram have successfully treated a 14-month-old baby from Kenya who was suffering from the extremely rare and life-threatening Pearson Syndrome.

In a groundbreaking study, researchers at McMaster University have identified a potential treatment for Sandhoff and Tay-Sachs diseases—two rare, often fatal lysosomal storage disorders that cause ...

Chhatrapati Sambhajinagar (Maharashtra) [India], November 14: Medicover Hospitals has marked a significant milestone in healthcare by successfully performing First time in Marathwada a rare and ...

While typhoid fever is a rare illness in Canada, especially in non-travel-related cases, the event reminds us of the role ...